Haruo Shintaku   Toshihiro Ohura   Masaki Takayanagi   Shigeo Kure   Misao Owada   Yoichi Matsubara   Makoto Yoshino   Yoshiyuki Okano   Tetsuya Ito   Torayuki Okuyama   Kimitoshi Nakamura   Masafumi Matuo   Fumio Endo   Hiroyuki Ida   
Pediatrics international : official journal of the Japan Pediatric Society 63(1) 8-12 2021年1月
IMPORTANCE: Sapropterin hydrochloride, a natural coenzyme (6R-tetrahydrobiopterin) of phenylalanine hydroxylase, was first approved as a treatment for tetrahydrobiopterin deficiency in 1992 in Japan, and was then approved as a treatment for a tetr...